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Predictors of Final Visual Outcome in Patients With Leber Hereditary Optic Neuropathy Treated With Lenadogene Nolparvovec Gene Therapy.
Sergott Robert C, Carelli Valerio, Newman Nancy J, Biousse Valérie, Yu-Wai-Man Patrick, Vignal-Clermont Catherine et al.
Invest Ophthalmol Vis SciJul 20251 citationsClinical Trial
This study found that better baseline vision and thicker retinal nerve fiber and ganglion cell layers predict improved visual outcomes 1.5 years after gene therapy for LHON.