Leber Hereditary Optic Neuropathy Gene Therapy: Longitudinal Relationships Among Visual Function and Anatomical Measures.
Lam Byron L, Feuer William J, Porciatti Vittorio, Davis Janet L, Zheng D Diane, Vanner Elizabeth A et al.
Gene therapy for LHON showed asymptomatic eyes might be too advanced for neuroprotection, suggesting early intervention is key.